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Table 1:

Clinical characteristics and MDFRS scores

Patients with DMD (Range)Controls (Range)
Age at recruitment (mean) (yr)8.0 ± 1.2 (6–10)8.2 ± 1.4 (6–10)
Age at onset (mean) (yr)4.1 ± 1.8 (1–9)
Age at presentation (mean) (range) (yr)7.5 ± 1.4 (4–10)
Duration (mean) (mo)40.8 ± 25.2 (6–120)
MDFRS domains (mean)
 Mobility (maximum 36)24.35 ± 3.272 (15–30)
 Basic ADL (maximum 24)18.77 ± 2.547 (12–25)
 Arm function (maximum 28)22.07 ± 1.885 (19–25)
 Impairment (maximum 44)34.18 ± 3.568 (23–40)
 Total score (maximum 132)99.37 ± 10.55 (69–117)
  • Note:—ADL indicates activities of daily living; MDFRS, Muscular Dystrophy Functional Rating scale.