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Table 1: Clinical characteristics and MDFRS scores
Patients with DMD (Range) Controls (Range) Age at recruitment (mean) (yr) 8.0 ± 1.2 (6–10) 8.2 ± 1.4 (6–10) Age at onset (mean) (yr) 4.1 ± 1.8 (1–9) Age at presentation (mean) (range) (yr) 7.5 ± 1.4 (4–10) Duration (mean) (mo) 40.8 ± 25.2 (6–120) MDFRS domains (mean) Mobility (maximum 36) 24.35 ± 3.272 (15–30) Basic ADL (maximum 24) 18.77 ± 2.547 (12–25) Arm function (maximum 28) 22.07 ± 1.885 (19–25) Impairment (maximum 44) 34.18 ± 3.568 (23–40) Total score (maximum 132) 99.37 ± 10.55 (69–117)
Note:—ADL indicates activities of daily living; MDFRS, Muscular Dystrophy Functional Rating scale.